A Second Chance At
Sight
Wednesday, Apr 30 2008 | Author and
categories:
Andrew Goss
| NW tech news
In what could be a major milestone for gene therapy,
for the first time, researchers have used gene
therapy to improve vision in blind patients.
Homegrown (for VOXUS) Seattle’s Targeted
Genetics conducted part of the study of six patients
with an extremely rare form of blindness called
Leber's Congenital Amaurosis.
According to the
study which appears in the New
England Journal of Medicine, four of the six
people who received gene therapy had some vision
restored. If this test is successful on a larger
scale, researchers say it could help people with
more common types of blindness.
Macular degeneration, the leading
cause of blindness for those under 20 years old
in the United States, affects 1.25 million
Americans; the number is expected to grow to 3
million by 2020 as the population continues to
age.
Gene therapy involves replacing defective genes with
normal versions. The research marks a major milestone
for gene therapy, a discipline many scientists find
promising but so far has failed to produce a
marketable product in the U.S.
-posted by Andrew